Zolgensma – The world’s most expensive drug.
Novartis’s Biologics License Application (BLA) for Zolgensma, designed to tackle the genetic root cause of spinal muscular atrophy (SMA) Type 1, a deadly neuromuscular disease, was accepted by the FDA. According to Pharmaceutical daily news, SMA is caused by a defective or missing SMN1 gene, and without a functional SMN1 gene, infants with SMA Type…